Molecule of the Month May 2015 |
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Functional Correction in Mouse Models of Muscular Dystrophy Using Exon-Skipping Tricyclo-DNA Oligomers | ||
It is shown that systemic delivery of tcDNA promotes a high degree of rescue of dystrophin expression in skeletal muscles, the heart and, to a lesser extent, the brain.
This work was carried out in the group of Prof. Christian Leumann. References:
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